Genetic Diseases

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Trial underway for liver disease-causing genetic disorder treatment

December 18, 2019

Value-based agreements for acute hepatic porphyria therapy Givlaari launch

November 26, 2019
Alnylam Pharmaceuticals announced a new and enhanced framework for value-based agreements designed to provide access to the recently FDA-approved Givlaari for patients…
FDA News

FDA approves Givlaari, first treatment for acute hepatic porphyria

November 20, 2019
The FDA approved Givlaari for the treatment of adults with acute hepatic porphyria, a rare genetic disorder that leads to buildup of toxic porphyrin molecules that form…
Meeting News

National Liver Conference to cover ‘tsunami’ of new data on liver disease

October 24, 2019
SAN ANTONIO — The National Liver Congress will convene October 25th, providing a broad scientific program and exhibit of products and services important for all…
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